CRISPR Gene Therapy Gains Regulatory Approvals for Hemoglobinopathies and Hemophilia
Words by Yuriy Poteshkin, MD, phD
The year 2025 witnessed consolidation of CRISPR-Cas9 and AAV-mediated gene therapy as curative options for inherited blood disorders, with expanding clinical evidence for sickle cell disease,...
Dec 31, 2025Read more
trends 2025CRISPR-Cas9gene therapy